Companies related to Rare Disease

We Empower the Life Science, FMCG, and Financial industries with innovative solutions.

Serving Patients, Improving Lives

Research...for a healthy future

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Our mission is to treat and cure FA by marshaling and focusing global resources and relationships.

Science for Life

Baylor Genetics pioneered the history of genetic testing. Now, we’re leading the way in precision medicine.

Advancing peptides for the treatment of rare endocrine and related diseases

Providing Pharma & Biopharma with RWD & AI-Driven Insights on Patient Populations Affected by Speciality & Rare Diseases

Empowering Health: Top Tier Pharmaceutical Distribution since 1952 - Serving the Jordanian Market with Excellence

In Pursuit of Answers

Where Empathy Meets Science to Accelerate Life Sciences Research

Alone we are rare. Together we are strong.®

Your Leader in Rare Disease and Complex Therapy Programs

Pharmaceutical Company & Service Partner

AI Accelerated Preventative Healthcare

As a leading full-service global CRO, we work to create solutions that advance new treatments from discovery to reality.

The standard of NAD measuring.

As a leading full-service global CRO, we work to create solutions that advance new treatments from discovery to reality.

MCRI is dedicated to making discoveries to prevent and treat common and rare childhood conditions.

An integrative analytic platform connecting phenotypes to genotypes across species, bridging basic and applied research.

Accelerating Drug, Biologic and Medical Device Clinical Development

Quality development & manufacturing. Customized solutions.

Better Science, Better Lives.

The Premier Rare Disease Company in Israel. We Deliver Rare Dedication to Wellness.

Full-Service CRO delivering excellence in early stage clinical research, from Phase I & HAL trials to BE/BA studies.

Providing relief to patients with unmet medical needs in select specialty and rare diseases.

Through research, technology and collaboration, we make medical breakthroughs for those with NMOSD. Next up: CURES.

Building a better future for everyone.

Unsere Philosophie ist das Schlüssel-Schloss-Prinzip: für langfristig erfolgreiche Kunden- und Kandidatenbeziehungen.

Enabling a better future for people with rare immune disorders

We’re Built for Biotech℠, dedicated to helping today’s top innovators turn big ideas into life-changing treatments.

A biopharmaceutical company focused on delivering Medicines that Make a Difference® in patients’ and caregivers’ lives.

Leading the fight to treat and cure Tay-Sachs, Canavan, GM1, and Sandhoff diseases.

Going Beyond Every Day

Global fieldwork management, pharma, biotech and healthcare

Rare but not alone

Better Health, Brighter Future | Santé meilleure, avenir prometteur

Transformation in Sight

Leading patient advocacy organization working to eliminate the challenges of rare disease. #CareAboutRARE #RareDisease

Leading patient advocacy organization working to eliminate the challenges of rare disease. #CareAboutRARE #RareDisease

Clintec is an IQVIA company.

Decoding Biology to Radically Improve Lives

FOR RARE, BY RARE

FOR RARE, BY RARE

Developing best-in-class curative gene therapies for rare disorders.

Working together to find a cure

Transforming healthcare connections

Great Science Deserves Great People.

Great Science Deserves Great People.

Great Science Deserves Great People.

Support + Educate + Advocate - Preemies & Pros from Pregnancy to the Adult Years

PNRI unravels the powerful mysteries of genetics to drive future medical breakthroughs.

AI for Faster Rare Disease Diagnosis | Scalable PaaS Solutions for Hospitals & Pharma

Clinical research value chain organization (trial management, SMO, warehousing, supply, sourcing and distribution)

Kyowa Kirin International | Making people smile | www.KyowaKirinInternational.com

Finding Innovative Global Health Solutions For Today and Tomorrow Through Clinical Research. # OrganicCRO

A transformative idea for transformative medicines

Bringing expertise to deliver medicines our world can trust.

Leading European Umbrella Association for Pulmonary Hypertension | Join Us in Empowering PH Patients!

Independent Thinking. Individualized Care.

Genomic intelligence for clinical diagnostics and precision medicine development

A relentless force in finding a cure and improving the lives of people affected by scleroderma.

Creating transformative therapies for genetic diseases that improve lives

Rare Disease Consulting and Service Organization

Savara is a clinical stage biopharmaceutical company focused on rare respiratory diseases.

Global "networked" consultancy specializing in customer engagement & digital transformation in Health + Life Sciences.

Bringing life changing treatments to people with genetic disease, regardless of prevalence or commercial interest

We Connect- We Inform - We Collaborate

Clinical-stage lentiviral gene therapy company, powered by plato®. Our vision: bring personalized gene therapy worldwide

Komtur delivers comprehensive healthcare solutions that connect pharmaceutical innovations with patients.

Global Multi-Award-Winning Access Experts for Orphan Drugs, Cell and Gene Therapies

Your partner for bringing science to life.

The world’s largest research-focused patient advocacy organization for facioscapulohumeral muscular dystrophy (FSHD) .

19 years connecting talent with life sciences companies

Your Compassionate Health Ally

Rare Solutions, Extraordinary Results.

We push the boundaries of science to deliver life-changing medicines.

Die Schweizerische Neurologische Gesellschaft ist der Berufsverband der Fachärztinnen und Fachärzte für Neurologie

Treating Neurodegenerative Disease by Restoring Autophagy

Serving patients across Middle East, North Africa & Turkey through collaborative partnerships.

Providing solutions to better navigate the inherent challenges of rare and specialty disease

Clinical Artificial Intelligence to improve diagnosis, management and research of Rare and Genetic Disease

Helping healthcare companies envision the future by generating customer insights to guide commercial success

STAR, a 501(c)3 non-profit, is dedicated to Salla disease research, treatment, education, awareness & family networks.

Connecting Families - Raising Awareness - Building Futures

Your partner of choice for advancing rare disease research

Kyowa Kirin North America is a specialty pharmaceutical company dedicated to making a profound impact on patient lives.

On a mission to improve your experience living with a chronic health condition

🔹 Premier Positions. Premier Talent. Premier Pharma. 🔹

An innovative gene editing company discovering and developing curative treatments for genetic diseases

Pioneering Cures Through Collaborative Computing

Pioneering Cures Through Collaborative Computing

International Pharmaceutical Group Certified B Corp

Patient Lifestyle and Disease Data Interactium (PaLaDIn)

Changing patients' lives everyday.

The Evolution of Clinical Research

Excellence in Ophthalmic Research

ESG Impact with an ROI!

Your One Answer Genetic testing for rare diseases made more efficient and more accessible

Specialist centre for clinical care and research in mitochondrial diseases at the National Hospital for Neurology