Companies related to Rare Disease

We Empower the Life Science, FMCG, and Financial industries with innovative solutions.

Where Empathy Meets Science to Accelerate Life Sciences Research

Advancing peptides for the treatment of rare endocrine and related diseases

Serving Patients, Improving Lives

Baylor Genetics pioneered the history of genetic testing. Now, we’re leading the way in precision medicine.

Research...for a healthy future

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Our mission is to treat and cure FA by marshaling and focusing global resources and relationships.

Science for Life

AI Accelerated Preventative Healthcare

Pharmaceutical Company & Service Partner

Providing Pharma & Biopharma with RWD & AI-Driven Insights on Patient Populations Affected by Speciality & Rare Diseases

Empowering Health: Top Tier Pharmaceutical Distribution since 1952 - Serving the Jordanian Market with Excellence

In Pursuit of Answers

MCRI is dedicated to making discoveries to prevent and treat common and rare childhood conditions.

Unsere Philosophie ist das Schlüssel-Schloss-Prinzip: für langfristig erfolgreiche Kunden- und Kandidatenbeziehungen.

As a leading full-service global CRO, we work to create solutions that advance new treatments from discovery to reality.

As a leading full-service global CRO, we work to create solutions that advance new treatments from discovery to reality.

Accelerating Drug, Biologic and Medical Device Clinical Development

The standard of NAD measuring.

Alone we are rare. Together we are strong.®

Your Leader in Rare Disease and Complex Therapy Programs

An integrative analytic platform connecting phenotypes to genotypes across species, bridging basic and applied research.

Quality development & manufacturing. Customized solutions.

Enabling a better future for people with rare immune disorders

A biopharmaceutical company focused on delivering Medicines that Make a Difference® in patients’ and caregivers’ lives.

The Premier Rare Disease Company in Israel. We Deliver Rare Dedication to Wellness.

Better Science, Better Lives.

Full-Service CRO delivering excellence in early stage clinical research, from Phase I & HAL trials to BE/BA studies.

Providing relief to patients with unmet medical needs in select specialty and rare diseases.

FOR RARE, BY RARE

FOR RARE, BY RARE

Support + Educate + Advocate - Preemies & Pros from Pregnancy to the Adult Years

We’re Built for Biotech℠, dedicated to helping today’s top innovators turn big ideas into life-changing treatments.

Building a better future for everyone.

Going Beyond Every Day

Leading the fight to treat and cure Tay-Sachs, Canavan, GM1, and Sandhoff diseases.

Through research, technology and collaboration, we make medical breakthroughs for those with NMOSD. Next up: CURES.

Transformation in Sight

Clintec is an IQVIA company.

Global fieldwork management, pharma, biotech and healthcare

Leading patient advocacy organization working to eliminate the challenges of rare disease. #CareAboutRARE #RareDisease

Leading patient advocacy organization working to eliminate the challenges of rare disease. #CareAboutRARE #RareDisease

Better Health, Brighter Future | Santé meilleure, avenir prometteur

Decoding Biology to Radically Improve Lives

Rare but not alone

Transforming healthcare connections

Clinical research value chain organization (trial management, SMO, warehousing, supply, sourcing and distribution)

PNRI unravels the powerful mysteries of genetics to drive future medical breakthroughs.

Developing best-in-class curative gene therapies for rare disorders.

Working together to find a cure

Finding Innovative Global Health Solutions For Today and Tomorrow Through Clinical Research. # OrganicCRO

AI for Faster Rare Disease Diagnosis | Scalable PaaS Solutions for Hospitals & Pharma

A transformative idea for transformative medicines

Great Science Deserves Great People.

Great Science Deserves Great People.

Great Science Deserves Great People.

Bringing expertise to deliver medicines our world can trust.

On a mission to improve your experience living with a chronic health condition

Kyowa Kirin International | Making people smile | www.KyowaKirinInternational.com

Leading European Umbrella Association for Pulmonary Hypertension | Join Us in Empowering PH Patients!

We are a late-stage biopharmaceutical company focused on developing & commercializing products to treat rare diseases

Helping healthcare companies envision the future by generating customer insights to guide commercial success

Creating transformative therapies for genetic diseases that improve lives

Genomic intelligence for clinical diagnostics and precision medicine development

Kyowa Kirin North America is a specialty pharmaceutical company dedicated to making a profound impact on patient lives.

Specialist centre for clinical care and research in mitochondrial diseases at the National Hospital for Neurology

Bringing life changing treatments to people with genetic disease, regardless of prevalence or commercial interest

Your Compassionate Health Ally

Clinical Artificial Intelligence to improve diagnosis, management and research of Rare and Genetic Disease

Clinical-stage lentiviral gene therapy company, powered by plato®. Our vision: bring personalized gene therapy worldwide

Komtur delivers comprehensive healthcare solutions that connect pharmaceutical innovations with patients.

Global "networked" consultancy specializing in customer engagement & digital transformation in Health + Life Sciences.

International Pharmaceutical Group Certified B Corp

Independent Thinking. Individualized Care.

The world’s largest research-focused patient advocacy organization for facioscapulohumeral muscular dystrophy (FSHD) .

Global Multi-Award-Winning Access Experts for Orphan Drugs, Cell and Gene Therapies

Providing solutions to better navigate the inherent challenges of rare and specialty disease

Serving patients across Middle East, North Africa & Turkey through collaborative partnerships.

Die Schweizerische Neurologische Gesellschaft ist der Berufsverband der Fachärztinnen und Fachärzte für Neurologie

Innovative Solutions to Achieve Market Access Objectives

A global full-service CRO.

Changing patients' lives everyday.

We Connect- We Inform - We Collaborate

Your partner for bringing science to life.

Rare Disease Consulting and Service Organization

We push the boundaries of science to deliver life-changing medicines.

19 years connecting talent with life sciences companies

ESG Impact with an ROI!

A relentless force in finding a cure and improving the lives of people affected by scleroderma.

Your partner of choice for advancing rare disease research

Savara is a clinical stage biopharmaceutical company focused on rare respiratory diseases.

Your One Answer Genetic testing for rare diseases made more efficient and more accessible

Franklin harnesses the power of its community to enable actionable insights, serving professionals at the point of care

Patient Lifestyle and Disease Data Interactium (PaLaDIn)

Connecting Families - Raising Awareness - Building Futures

Excellence in Ophthalmic Research

Treating Neurodegenerative Disease by Restoring Autophagy

Unistel Medical Laboratories is a leading human and animal genetic testing centre.

Rare Solutions, Extraordinary Results.